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Jason A Gilbert
Jason A Gilbert
Alnylam Pharmaceuticals
Transthyretin
Amyloidosis
Biochemistry
Small interfering RNA
Biology
3
Papers
8
Citations
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siRNAs containing 2'-fluorinated Northern-methanocarbacyclic (2'-F-NMC) nucleotides: in vitro and in vivo RNAi activity and inability of mitochondrial polymerases to incorporate 2'-F-NMC NTPs.
2021
Nucleic Acids Research
Masaaki Akabane-Nakata
Namrata D. Erande
Pawan Kumar
Rohan Degaonkar
Jason A Gilbert
June Qin
Martha Mendez
Lauren Blair Woods
Yongfeng Jiang
Maja M. Janas
Derek K OFlaherty
Ivan Zlatev
Mark K. Schlegel
Shigeo Matsuda
Martin Egli
Muthiah Manoharan
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Citations (1)
Nonclinical Safety Profile of Revusiran, a 1st-Generation GalNAc-siRNA Conjugate for Treatment of Hereditary Transthyretin-Mediated Amyloidosis
2019
Nucleic Acid Therapeutics
Jessica E. Sutherland
Julia Hettinger
Amy Chan
Jason A Gilbert
Garvin Warner
Wendell P Davis
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Citations (6)
Plasma Proteome Analysis of Patients with Hereditary Transthyretin-Mediated (hATTR) Amyloidosis Establishes Neurofilament Light Chain (NfL) as a Biomarker of Disease and Treatment Response
2019
medRxiv
Simina Ticau
Gautham V Sridharan
Shira Tsour
William Cantley
Amy Chan
Jason A Gilbert
David Erbe
Emre Aldinc
Mary M. Reilly
David Adams
Michael Polydefkis
Kevin Fitzgerald
Akshay Vaishnaw
Paul Nioi
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Citations (1)
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