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Javier Poyatos-Garcia
Javier Poyatos-Garcia
Biology
Cas9
Exon
Exon skipping
Dystrophin
2
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Musashi-2 contributes to myotonic dystrophy muscle dysfunction by promoting excessive autophagy through miR-7 biogenesis repression.
2021
Molecular therapy. Nucleic acids
María Sabater-Arcis
Ariadna Bargiela
Nerea Moreno
Javier Poyatos-Garcia
Juan J. Vílchez
Ruben Artero
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A CRISPR/Cas9-Based Approach For Editing Immortalised Human Myoblasts To Model Duchenne Muscular Dystrophy In Vitro
2020
bioRxiv
Patricia Soblechero Martin
Edurne Albiasu-Arteta
Aina Anton-Martinez
I. García Jiménez
Gabriela Gonzalez-Iglesias
Irene Larranaga-Aiestaran
Andrea Lopez Martinez
Javier Poyatos-Garcia
E. Ruiz del Yerro
Federico Gonzalez
Virginia Arechavala-Gomeza
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