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Development of a stem cell gene therapy for Sanfilippo syndrome type B
Development of a stem cell gene therapy for Sanfilippo syndrome type B
2017
Don Clarke
Valentina Sanguez
Shih Kan
Steven Lee
Michelina Iacovino
Patricia I. Dickson
Keywords:
Biology
Stem cell
Sanfilippo syndrome
Cancer research
Genetic enhancement
Bioinformatics
Diabetes mellitus
Genetics
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