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Bochra Mlaya
Bochra Mlaya
French Institute of Health and Medical Research
Promoter
γ globin
Binding site
Fetal hemoglobin
Molecular biology
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Editing the LRF Repressor Binding Site in the γ-Globin Promoters Induces Therapeutically Relevant Fetal Hemoglobin Levels for the Treatment of β-Hemoglobinopathies
2020
Blood
Giacomo Frati
Panagiotis Antoniou
Giulia Hardouin
Bochra Mlaya
Leslie Weber
Tristan Felix
Antonio Casini
Marion Rosello
Anne Chalumeau
Mario Amendola
Adrian J. Thrasher
Giandomenico Turchiano
Filippo Del Bene
Wassim El Nemer
Anna Cereseto
Jean-Paul Concordet
Carine Giovannangeli
Marina Cavazzana
Annarita Miccio
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