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Lucy Crockett
Lucy Crockett
BioMarin Pharmaceutical
Antibody
Biology
Virus
Pharmacodynamics
Genetic enhancement
5
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32
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Impact of Pre-Existing Immunity on the Non-Clinical Pharmacodynamics of AAV5-Based Gene Therapy
2019
Molecular therapy. Methods & clinical development
Brian Long
Krystal Sandza
Jennifer Holcomb
Lucy Crockett
Greg Hayes
Jeremy Arens
Carlos Fonck
Laurie Tsuruda
Becky Schweighardt
Charles A. O'Neill
Stephen Zoog
Christian Vettermann
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Citations (20)
Impact of Pre-Existing Immunogenicity to AAV on Vector Transduction By Bmn 270, an AAV5-Based Gene Therapy Treatment for Hemophilia A
2017
Blood
Brian Long
Krystal Sandza
Jennifer Holcomb
Juli Pherarolis
Lucy Crockett
Lillian Falese
Greg Hayes
Jeremy Arens
Charles A. O'Neill
Nancy Pryer
Carlos Fonck
Stephen Zoog
Christian Vettermann
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A comparison of pharmacological activity of original and new production lots of BMN 701 using glycogen clearance in a mouse model of Pompe disease
2014
Molecular Genetics and Metabolism
Jeff Peng
Rhea Cahayag
Lucy Crockett
Charles A. O'Neill
Jon Lebowitz
Laurie Tsuruda
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Comparison of Neutralizing Antibody Assays for Receptor Binding and Enzyme Activity of the Enzyme Replacement Therapeutic Naglazyme® (Galsulfase)
2008
Aaps Journal
Joleen White
Lisa Argento Martell
William S. Prince
Ryan Boyer
Lucy Crockett
Christopher Cox
Andrea Van Tuyl
Allora I. Aguilera
Erik Foehr
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Citations (10)
1