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Carlos J. Miranda
Carlos J. Miranda
Bone marrow
Genetics
Glucocerebroside
Diabetes mellitus
Transgene
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Liver directed AAV gene therapy to treat Gaucher disease
2019
Molecular Genetics and Metabolism
Carlos J. Miranda
Jenny McIntosh
Azadeh Kia
Miriam Canavese
Jonathan Foley
Doyoung Lee
Paniz Hosseini
Jey Jeyakumar
Rose Sheridan
Romuald Corbau
Amit C. Nathwani
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