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Elisabet Ohlin Sjöström
Elisabet Ohlin Sjöström
Mucopolysaccharidosis Type IIIA
Pathology
Neuroinflammation
Mucopolysaccharidosis
Genetics
2
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7
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0
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Intravenous delivery of a chemically modified sulfamidase efficiently reduces heparan sulfate storage and brain pathology in mucopolysaccharidosis IIIA mice
2019
Molecular genetics and metabolism reports
Susanne Gustavsson
Elisabet Ohlin Sjöström
Agneta Tjernberg
Juliette Janson
Ulrica Westermark
Tommy Andersson
Åsa Makower
Erik Arnelöf
Gudrun Andersson
Jan Svartengren
Carina Ekholm
Stefan Svensson Gelius
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Citations (7)
Behavioral and histological hallmarks of a mucopolysaccharidosis type IIIA mouse model
2019
Molecular Genetics and Metabolism
Vera Niederkofler
Ewald Auer
David Amschl
Joerg Neddens
Elisabet Ohlin Sjöström
Susanne Gustavsson
Birgit Hutter-Paier
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