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Matthew O’Neal
Matthew O’Neal
Marshall University
Oncology
Internal medicine
Disease
Medicine
Cerliponase alfa
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Cerliponase alfa for CLN2 disease, a promising therapy
2020
Expert opinion on orphan drugs
Shawn C. Aylward
Jonathan Pindrik
Nicolas J. Abreu
W. Bruce Cherny
Matthew O’Neal
Emily de los Reyes
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