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Johannes Lengler
Johannes Lengler
Takeda Pharmaceutical Company
Genetic enhancement
Gene
Secretion
Adeno-associated virus
Molecular biology
3
Papers
6
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0
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2024
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Development of an in vitro biopotency assay for an AAV8 hemophilia B gene therapy vector suitable for clinical product release
2020
Molecular therapy. Methods & clinical development
Johannes Lengler
Sogue Coulibaly
Bernadette Gruber
Reinhard Ilk
Josef Mayrhofer
Friedrich Scheiflinger
Werner Hoellriegl
Falko G. Falkner
Hanspeter Rottensteiner
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Citations (4)
Minimal Essential Human Factor VIII Alterations Enhance Secretion and Gene Therapy Efficiency
2020
Molecular therapy. Methods & clinical development
Wenjing Cao
Biao Dong
Franziska Horling
Jenni Firrman
Johannes Lengler
Matthias Klugmann
Maurus de la Rosa
Wenman Wu
Qizhao Wang
Hongying Wei
Adrian R. Moore
Sean Roberts
Carmen J. Booth
Werner Hoellriegl
Dong Li
Barbara Konkle
Carol H. Miao
Birgit M. Reipert
Friedrich Scheiflinger
Hanspeter Rottensteiner
Weidong Xiao
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Citations (2)
The Factor VIII Variant X5 Enhances Hemophilia a Gene Therapy Efficiency By Its Improved Secretion
2019
Blood
Franziska Horling
Johannes Lengler
Wenjing Cao
Biao Dong
Bagirath Gangadharan
Maurus de la Rosa
Werner Hoellriegl
Birgit M. Reipert
Friedrich Scheiflinger
Weidong Xiao
Hanspeter Rottensteiner
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