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Claudio Semplicini
Claudio Semplicini
Disease
Medicine
Cohort
Enzyme replacement therapy
FEV1/FVC ratio
2
Papers
20
Citations
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Investigating myopathic causes of rhabdomyolysis
2017
Claudio Semplicini
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Effect of enzyme replacement therapy with alglucosidase alfa (Myozyme®) in 12 patients with advanced late-onset Pompe disease
2017
Molecular Genetics and Metabolism
Constantinos Papadopoulos
David Orlikowski
Hélène Prigent
Barbara Perniconi
N. Taouagh
Arnaud Lacour
C. Tard
A. Furby
J. Praline
Guilhem Solé
Claudio Semplicini
P. Kaminsky
Bruno Eymard
D. Hamroun
Pascal Laforět
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Citations (20)
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