Old Web
English
Sign In
Acemap
>
authorDetail
>
Laura Lee
Laura Lee
Great Ormond Street Hospital
Disease
Cerliponase alfa
Neuronal Ceroid Lipofuscinosis Type 2
Medicine
clinical course
2
Papers
3
Citations
0
KQI
Citation Trend
Filter By
Interval:
1900~2024
1900
2024
Author
Papers (2)
Sort By
Default
Most Recent
Most Early
Most Citation
No data
Journal
Conference
Others
Investigating health-related quality of life in rare diseases: a case study in utility value determination for patients with CLN2 disease (neuronal ceroid lipofuscinosis type 2).
2021
Orphanet Journal of Rare Diseases
Paul Gissen
Nicola Specchio
Andrew Olaye
Mohit Jain
Thomas Butt
W Ghosh
Benjamin Ruban-Fell
A. Griffiths
Charlotte Camp
Zlatko Sisic
Christoph Schwering
Eva Wibbeler
Marina Trivisano
Laura Lee
Miriam Nickel
Amanda Mortensen
Angela Schulz
Show All
Source
Cite
Save
Citations (0)
Cerliponase Alfa for the Treatment of Atypical Phenotypes of CLN2 Disease: A Retrospective Case Series.
2020
Journal of Child Neurology
Eva Wibbeler
Raymond Y. Wang
Emily de los Reyes
Nicola Specchio
Paul Gissen
Norberto Guelbert
Miriam Nickel
Christoph Schwering
Lenora Lehwald
Marina Trivisano
Laura Lee
Gianni Amato
Jessica Cohen-Pfeffer
Renée Shediac
Fernanda Leal-Pardinas
Angela Schulz
Show All
Source
Cite
Save
Citations (3)
1