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Amy Strong Martin
Amy Strong Martin
University of California, Los Angeles
Duchenne muscular dystrophy
Genetic enhancement
Placebo
Internal medicine
Endocrinology
2
Papers
11
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0
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Patients' and caregivers' maximum acceptable risk of death for non-curative gene therapy to treat Duchenne muscular dystrophy
2021
Molecular Genetics & Genomic Medicine
Holly L. Peay
Ryan Fischer
Brennan Mange
Ryan S. Paquin
Edward C. Smith
Alesia Sadosky
Leo Russo
Valeria Ricotti
Colin Rensch
Carl Morris
Amy Strong Martin
Annie Ganot
Katherine Beaverson
Carol Mansfield
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Priorities when deciding on participation in early-phase gene therapy trials for Duchenne muscular dystrophy: a best–worst scaling experiment in caregivers and adult patients
2019
Orphanet Journal of Rare Diseases
Ryan S. Paquin
Ryan Fischer
Carol Mansfield
Brennan Mange
Katherine Beaverson
Annie Ganot
Amy Strong Martin
Carl Morris
Colin Rensch
Valeria Ricotti
L Russo
Alesia Sadosky
Edward C. Smith
Holly L. Peay
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Citations (11)
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