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Jenn Daily
Jenn Daily
Endosome
Cancer research
Genetic enhancement
Mutation
Biology
2
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3
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PR001 gene therapy improved phenotypes in models of Parkinson’s disease with GBA1 mutation: Molecular and cell biology/endosomal‐lysosomal dysfunction
2020
Alzheimers & Dementia
Patty Sheehan
Laura D. Heckman
Tim Fenn
Li Chin Wong
Stuart Nelson
Swetha Garimalla
Jorge Haller
Jenn Daily
Jason Politi
Yong Dai
Franz Hefti
Asa Abeliovich
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Citations (2)
Preclinical development of PR006, a gene therapy for the treatment of frontotemporal dementia with progranulin mutations: Molecular and cell biology/endosomal‐lysosomal dysfunction
2020
Alzheimers & Dementia
Laura D. Heckman
Suzanne R. Burstein
Alissa Brandes
Li Chin Wong
Zhaohui Yang
Hsuan‐Ni Lin
Tim Fenn
Stuart Nelson
Zarah Aziz
Sid Kamalakaran
Swetha Garimalla
Jorge Haller
Jenn Daily
Jason Politi
Yong Dai
Franz Hefti
Asa Abeliovich
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Citations (1)
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