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Wendy S. Frankhuizen
Wendy S. Frankhuizen
Leiden University Medical Center
Muscular dystrophy
Molecular biology
Exon
Eteplirsen
Drisapersen
2
Papers
771
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Local Dystrophin Restoration with Antisense Oligonucleotide PRO051
2007
The New England Journal of Medicine
Judith C. T. van Deutekom
Anneke A.M. Janson
Ieke B. Ginjaar
Wendy S. Frankhuizen
Annemieke Aartsma-Rus
Mattie Bremmer-Bout
Johan T. den Dunnen
Klaas Koop
Anneke J. van der Kooi
Nathalie Goemans
Sjef J. de Kimpe
Peter F. Ekhart
Edna H. Venneker
Gerard Johannes Platenburg
Jan J. Verschuuren
Gert-Jan B. van Ommen
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Citations (715)
Protein studies in dysferlinopathy patients using llama-derived antibody fragments selected by phage display
2005
European Journal of Human Genetics
Yanchao Huang
Peter Verheesen
Andreas Roussis
Wendy S. Frankhuizen
Ieke B. Ginjaar
Faye Haldane
S. Laval
Louise V. B. Anderson
Theo Verrips
Rune R. Frants
Hans de Haard
Kate Bushby
Johan T. den Dunnen
Silvère M. van der Maarel
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Citations (56)
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