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R. Dhulipala
R. Dhulipala
Amicus Therapeutics
Biology
Disease
Diabetes mellitus
Pharmacological chaperone
Biochemistry
3
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G.P.11.05 The pharmacological chaperone AT2220 increases trafficking, processing, and cellular activity of acid α-glucosidase and is a potential new treatment for Pompe disease
2008
Neuromuscular Disorders
Allan C. Powe
John Flanagan
Richie Khanna
Xiaoyang Wu
W. Liang
R. Dhulipala
T. Yin
K. Tang
Rebecca Soska
Lee Pellegrino
S. Shao
Elfrida R. Benjamin
Kenneth J. Valenzano
Brandon Wustman
David J. Lockhart
Hung V. Do
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G.O. 7 Pharmacological chaperones as an alternate treatment for Pompe disease
2006
Neuromuscular Disorders
Brandon Wustman
Richie Khanna
Allan C. Powe
R. Dhulipala
Elfrida R. Benjamin
C.W. Pine
W. Liang
Kirsten Mascioli
Hui-Hwa Chang
Matthew J. Toth
P. Huertas
Kenneth J. Valenzano
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