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Valentina Sardone
Valentina Sardone
University College London
Duchenne muscular dystrophy
Dystrophin
Exon
Oligonucleotide
Sense (molecular biology)
1
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11
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A multicenter comparison of quantification methods for antisense oligonucleotide-induced DMD exon 51 skipping in Duchenne muscular dystrophy cell cultures
2018
PLOS ONE
Monika Hiller
Maria Sofia Falzarano
I. García Jiménez
Valentina Sardone
Ruurd C. Verheul
Linda Popplewell
Karen Anthony
E. Ruiz del Yerro
H. Osman
Jelle J. Goeman
Kamel Mamchaoui
George Dickson
Alessandra Ferlini
Francesco Muntoni
Annemieke Aartsma-Rus
Virginia Arechavala-Gomeza
Nicole A. Datson
Pietro Spitali
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Citations (11)
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