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K. Gelblin
K. Gelblin
Spinal muscular atrophy
Genetics
Diabetes mellitus
Biology
Pediatrics
2
Papers
14
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P.064 FIREFISH Part 1: 1-year results on motor function in infants with Type 1 spinal muscular atrophy (SMA) receiving risdiplam (RG7916)
2019
Canadian Journal of Neurological Sciences
T. Seabrook
Giovanni Baranello
L. Servais
John W. Day
Nicolas Deconinck
Eugenio Mercuri
Andrea Klein
Basil T. Darras
R. Masson
Heidemarie Kletzl
Y. Cleary
M. El-Khairi
Christian Czech
M. Gerber
C. Nguyen
K. Gelblin
Ksenija Gorni
Omar Khwaja
C Cabalteja
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Citations (4)
P.353FIREFISH Part 1: 16-month safety and exploratory outcomes of risdiplam (RG7916) treatment in infants with type 1 spinal muscular atrophy
2019
Neuromuscular Disorders
G. Baranello
L. Servais
John W. Day
Nicolas Deconinck
E. Mercuri
Andrea Klein
Basil T. Darras
Riccardo Masson
Heidemarie Kletzl
Yumi Cleary
M. El-Khairi
T. Seabrook
Christian Czech
Marianne Gerber
C. Nguyen
K. Gelblin
K. Gorni
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Citations (10)
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