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Steven##Fortucci
Steven##Fortucci
Enzyme
Chemistry
Molecular biology
Hyperammonemia
Enzyme assay
2
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9
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0
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Dual mRNA therapy restores metabolic function in long-term studies in mice with propionic acidemia.
2020
Nature Communications
Lei Jiang
Ji Sun Park
Ling Yin
Rodrigo Laureano
Eric Jacquinet
Jinsong Yang
Shi Liang
Andrea Frassetto
Jenny Zhuo
Xinhua Yan
Xuling Zhu
Steven##Fortucci
Kara Hoar
Cosmin Mihai
Christopher Tunkey
Vladimir Presnyak
Kerry Benenato
Christine M. Lukacs
Paolo Martini
Lin T. Guey
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Generation of a mouse model of Primary Hyperoxaluria Type 1 via CRISPR/Cas9 mediated gene editing
2019
Kimberly Ann Coughlan
Rajanikanth J Maganti
Andrea Frassetto
Christine DeAntonis
Meredith Wolfrom
Anne-Renee Graham
Shawn M. Hillier
Steven##Fortucci
Hoor Al Jandal
Sue-Jean Hong
Paloma H. Giangrande
Paolo Martini
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