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Expanded access program with Nusinersen in SMA type I in Italy: Strengths and pitfalls of a successful experience
Expanded access program with Nusinersen in SMA type I in Italy: Strengths and pitfalls of a successful experience
2017
Sonia Messina
Marika Pane
V. Sansone
Claudio Bruno
Michela Catteruccia
Giuseppe Vita
Concetta Palermo
Emilio Albamonte
Marina Pedemonte
Enrico Bertini
Luca Binetti
Eugenio Mercuri
Daniela Lauro
Anita Pallara
Simona Spinoglio
Maria Letizia Solinas
Grazia Zappa
Francesca Penno
Cristina Ponzanelli
Jacopo Luca Casiraghi
Marcello Villanova
D. Tiziano
Anna Mandelli
Chiara Mastella
Alberto Fontana
Anna Ambrosini
Daniela Leone
Roberto De Sanctis
Nicola Forcina
M. Piastra
Orazio Genovese
Alessandro Pedicelli
Maria Sframeli
Antonio Versaci
Imma Rulli
Eloisa Gitto
Cristina Faraone
Stefania La Foresta
Maria Macri
Adele DAmico
Giulia Colia
Anna Maria Bonetti
Adelina Carlesi
Renato Cutrera
Maria Beatrice Chiarini
Marta Ferretti
Alberto Garaventa
Giovanni Montobbio
Carlo Gandolfo
Valentina Iurilli
Paola Tacchetti
Emilia Bobeica
Alessia D'Agostino
Alice Pirola
Sara Luppone
Elisa De Mattia
Elisa Falcier
Fabrizio Rao
Fausto Fedeli
Luca Mancini
Paolo Stoia
Maurizio Heinen
Valeria Cozzi
Beatrice Travaglia
Emma Mizzotti
Keywords:
Biology
SMA*
Medical education
Genetics
Expanded access
Nusinersen
Correction
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