Efficacy and Safety of Asfotase Alfa in Infants and Young Children With Hypophosphatasia: a Phase 2 Open-Label Study.

This study was sponsored by Alexion Pharmaceuticals, Inc. (Boston, MA, USA). The study was also supported, in part, by the National Center for Advancing Translational Sciences, National Institutes of Health (NIH), through University of California, San Francisco–Clinical and Translational Science Institute (UCSF–CTSI) Grant Number UL1 TR000004 (to P.H.)