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Antisense oligonucleotide treatment in CEP290‐related leber congenital amaurosis
Antisense oligonucleotide treatment in CEP290‐related leber congenital amaurosis
2019
Bart P. Leroy
Artur V. Cideciyan
Samuel G. Jacobson
Arlene V. Drack
Allen C. Ho
Alexandra V. Garafalo
Alejandro J. Roman
Michael R. Schwartz
Patricia Biasutto
Wilma de Wit
Michael E. Cheetham
Peter Adamson
David Rodham
Aniz Girach
Julie De Zaeytijd
Caroline Van Cauwenbergh
Stephen R. Russell
Keywords:
Surgery
Leber congenital amaurosis
Medicine
Bioinformatics
Sense (molecular biology)
Oligonucleotide
Diabetes mellitus
antisense oligonucleotide
Correction
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