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Cell Penetrating peptide-conjugated Morpholino rescues SMA in a symptomatic preclinical model
Cell Penetrating peptide-conjugated Morpholino rescues SMA in a symptomatic preclinical model
2020
E Pagliari
M. Bersani
Mafalda Rizzuti
A. Bordoni
Domenica Saccomanno
H.M. Moulton
Nereo Bresolin
Giacomo P. Comi
S Corti
Monica Nizzardo
Keywords:
Conjugated system
Cell-penetrating peptide
Cell biology
Chemistry
Morpholino
SMA*
Correction
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