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Design and Characterization of FLT210, a Potent Next Generation AAV-hFVIII Vector Candidate
Design and Characterization of FLT210, a Potent Next Generation AAV-hFVIII Vector Candidate
2019
Azadeh Kia
Fabrizio Comper
Samantha Correia
Caterina Casari
Segen Negash
María Portillo
Jalpa Pandya
Tihomir Dodev
Andreas Schulze
Florian Sonntag
Renee Kober
Clément Cocita
Elisa Chisari
Rebecca Alade
Erald Shehu
Jey Jeyakumar
Jaminder Khinder
Jonathan H. Foley
Allison P Dane
Jenny McIntosh
Hattie Ollerton
Olivier D. Christophe
Cécile V. Denis
Romuald Corbau
Keywords:
Computational biology
Medicine
Immunology
Molecular biology
host organism
Open reading frame
Gene
Genome
Capsid
Plasmid
Genetic enhancement
Transgene
Correction
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