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GAA deficiency in Pompe disease is alleviated by exon inclusion in iPS cell-derived skeletal muscle cells
GAA deficiency in Pompe disease is alleviated by exon inclusion in iPS cell-derived skeletal muscle cells
2018
Pim Pijnappel
Erik van der Wal
Atze J. Bergsma
Holm Zaehres
Hans R. Schöler
Ans T. van der Ploeg
Marcos J. Araúzo-Bravo
Keywords:
Induced pluripotent stem cell
Exon
Internal medicine
Disease
Endocrinology
GAA Deficiency
Skeletal muscle
Medicine
Correction
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