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Eliglustat, an Investigational Oral Therapy for Gaucher Disease Type 1 (GD1): Updated Phase 2 Results
Eliglustat, an Investigational Oral Therapy for Gaucher Disease Type 1 (GD1): Updated Phase 2 Results
2012
M. Judith Peterschmitt
Elena Lukina
Nora Watman
Marta Dragosky
Marcelo Iastrebner
Gregory M. Pastores
Elsa Avila Arreguin
Mici Phillips
Hanna Rosenbaum
Elena Sysoeva
Rasha Aguzzi
Leorah Ross
Ana Cristina Puga
Keywords:
Eliglustat
Disease
Biology
Diabetes mellitus
oral therapy
Genetics
Internal medicine
Correction
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