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Optogenetics in the Clinic: PIONEER, a Phase 1/2a Gene Therapy Program for Non-Syndromic Retinitis Pigmentosa
Optogenetics in the Clinic: PIONEER, a Phase 1/2a Gene Therapy Program for Non-Syndromic Retinitis Pigmentosa
2020
Joseph N. Martel
Simona Degli Esposti
Elise Boulanger-Scemama
Francesco Galluppi
Elodie Vernadal
David Gray
Magali Taiel
Laure Blouin
José-Alain Sahel
Keywords:
Bioinformatics
Optogenetics
Genetic enhancement
Retinitis pigmentosa
non syndromic
Medicine
Correction
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