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Gene Therapy for Lad-I Immunodeficiency: Preclinical Evaluation of HSC Transduction Under Optimized GMP-Conditions
Gene Therapy for Lad-I Immunodeficiency: Preclinical Evaluation of HSC Transduction Under Optimized GMP-Conditions
2019
Elena Almarza
Cristina Mesa-Nuñez
Carlos Damian
María Fernández García
Begoña Diez Cabezas
M. Luz Lozano
Paula Rio
Rosa Yañez
Ken Law
Brian C. Beard
Jonathan D. Schwartz
Juan A. Bueren
Keywords:
Immunodeficiency
Genetic enhancement
Immunology
Medicine
Transduction (genetics)
pelvic inflammatory disease
Transplantation
Severe combined immunodeficiency
cyclic gmp
Immunologic Deficiency Syndromes
Cancer research
Correction
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