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In utero enzyme replacement therapy in fetuses with lysosomal diseases: A phase I clinical trial
In utero enzyme replacement therapy in fetuses with lysosomal diseases: A phase I clinical trial
2021
Marisa E. Schwab
Jennifer L. Cohen
Billie R. Lianoglou
Renata C. Gallagher
Juan M. Gonzalez-Velez
Teresa N. Sparks
Mary E. Norton
Michael H. Gelb
Tim Wood
Priya S. Kishnani
Paul Harmatz
Tippi C. MacKenzie
Keywords:
Phases of clinical research
Enzyme replacement therapy
Medicine
Physiology
In utero
Fetus
Correction
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