T.P.43 Enzyme replacement therapy in late-onset Pompe disease – A systematic literature review

An open label clinical pilot study of resveratrol as a treatment for Friedreich ataxia E.M. Yiu , R. Peverill , G. Tai , C. Stockley , J. Sarsero , M. EvansGalea , A. Churchyard , L. Corben , K. Lee , M.M. Ryan , M.B. Delatycki 9 Murdoch Childrens Research Institute, Bruce Lefroy Centre, Parkville, Australia; Southern Health, Cardiology Department, Melbourne, Australia; Australian Wine Research Institute, Clinical Pharmacology Department, Adelaide, Australia; Murdoch Childrens Research Institute, Parkville, Australia; SouthernHealth, Neurology Department, Melbourne, Australia; Murdoch Childrens Research Institute, Bruce Lefroy Centre for Genetic Health Research, Melbourne, Australia; Murdoch Childrens Research Institute, Clinical Epidemiology and Biostatistics Unit, Parkville, Australia; Royal Children’s Hospital Melbourne, Children’s Neuroscience Centre, Parkville, Australia; Murdoch Childrens Research Institute, Bruce Lefroy Centre for Genetic Health Research, Parkville, Australia