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First-in-human study of a liver-directed AAV gene therapy (FLT190) in Fabry disease
First-in-human study of a liver-directed AAV gene therapy (FLT190) in Fabry disease
2020
Derralynn Hughes
Niten Patel
Russell Kinch
Leanne Dronfield
Gerard Short
Rose Sheridan
Azadeh Kia
Jey Jeyakumar
Romuald Corbau
Amit C. Nathwani
Keywords:
Genetics
Diabetes mellitus
Genetic enhancement
Fabry disease
Bioinformatics
Biology
Human study
first in human
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