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Use of 2 hydroxypropyl-beta-cyclodextrin therapy in two adult Niemann Pick Type C patients.
Use of 2 hydroxypropyl-beta-cyclodextrin therapy in two adult Niemann Pick Type C patients.
2016
Ana García-Robles
María José Company-Albir
Juan Eduardo Megías-Vericat
María José Fernández-Megía
Francisco Pérez-Miralles
Eduardo López-Briz
Carmen Alcalá-Vicente
Inmaculada Galeano
Bonaventura Casanova
José Luis Poveda
Keywords:
Intrathecal
Physical therapy
Diabetes mellitus
2-Hydroxypropyl-beta-cyclodextrin
Toxicity
Pharmacology
Medicine
Beta-Cyclodextrins
Niemann–Pick disease, type C
Compassionate Use Trials
2 hydroxypropyl β cyclodextrin
Correction
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