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Dual-gRNA Approach With Limited Off-Target Effect Corrects C9ORF72 Repeat Expansion In Vivo
Dual-gRNA Approach With Limited Off-Target Effect Corrects C9ORF72 Repeat Expansion In Vivo
2021
Xuejiao Piao
Dawei Meng
Xue Zhang
Qiang Song
Hailong Lv
Yichang Jia
Keywords:
C9orf72
Cell biology
Dual (category theory)
Guide RNA
In vivo
Trinucleotide repeat expansion
Physics
Correction
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