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Theodora Markati
Theodora Markati
University of Oxford
Medicine
Genetic enhancement
antisense oligonucleotides
Genomic imprinting
Angelman syndrome
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Lessons Learned from Discontinued Clinical Developments in Duchenne Muscular Dystrophy.
2021
Frontiers in Pharmacology
Theodora Markati
Liesbeth De Waele
Urlike Schara-Schmidt
Laurent Servais
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